Experimental drug shows early promise against inherited form of ALS, trial indicates

A clinical trial has found evidence that the experimental drug tofersen lowers levels of a disease-causing protein in people with an inherited form of amyotrophic lateral sclerosis, or ALS, caused by mutations in the gene SOD1.

from Health & Medicine News -- ScienceDaily https://www.sciencedaily.com/releases/2020/07/200708174306.htm